Science and Research

Unpacking the anti-fibrotic arsenal: molecular mechanisms and therapeutic translation of MSC-derived exosomes in pulmonary fibrosis

Pulmonary fibrosis (PF) is a progressive, fatal interstitial lung disease with a dire prognosis and limited therapeutic options. Current standard-of-care anti-fibrotic agents (e.g., nintedanib and pirfenidone) offer only modest efficacy in slowing disease progression. Mesenchymal stem cell-derived exosomes (MSC-Exos) have recently emerged as a promising cell-free therapeutic strategy, boasting superior biocompatibility, low immunogenicity, enhanced biodistribution, and an innate tropism for injured tissues. Their potent anti-fibrotic effects are mediated through multiple mechanisms: targeted homing to fibrotic niches; reprogramming of dysregulated immune responses, notably by shifting macrophage polarization from a pro-inflammatory (M1) to an anti-inflammatory/reparative (M2) phenotype; suppression of pathological extracellular matrix deposition via inhibition of core fibrogenic pathways; and alleviation of endoplasmic reticulum stress in alveolar epithelial cells. This review systematically delineates the biological functions and molecular mechanisms underpinning the therapeutic actions of MSC-Exos in PF. We further evaluate completed and ongoing clinical trials (2014-2024), appraise the current translational landscape, and identify persistent challenges in drug development. Ultimately, this integrative analysis aims to define the mechanistic basis of MSC-Exos' efficacy, evaluate their clinical trajectory, and provide a strategic roadmap for their development into precision nanotherapeutics for PF.

  • Xiao, Y.
  • Hoorain, I.
  • Zhang, L.
  • Bellusci, S.
  • Jin, X.
  • Yang, H.
  • Zhang, J. S.

Keywords

  • *Exosomes/transplantation/metabolism/immunology
  • Humans
  • *Pulmonary Fibrosis/therapy/metabolism/immunology/pathology
  • Animals
  • *Mesenchymal Stem Cells/metabolism
  • Endoplasmic Reticulum Stress
  • drug delivery
  • exosomes
  • extracellular matrix
  • immune modulation
  • mesenchymal stem cells
  • pulmonary fibrosis
  • targeted therapy
Publication details
DOI: 10.3389/fimmu.2025.1725041
Journal: Front Immunol
Pages: 1725041 
Work Type: Review
Location: UGMLC
Disease Area: DPLD
Partner / Member: JLU
Access-Number: 41459489


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